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On Demand Video

Investigational New Drug, Device and Therapeutics Symposium

Friday, June 6, 2025
4:50 PM - 6:20 PM ET
Location: Floridian CD

Livestream

    Moderator(s)

  • Michael Callaghan, MD

    Medical Director
    Agios Pharmaceuiticals
    Bloomfield Hills, Michigan, United States

Learning Objectives:

  • Understand the role of pyruvate kinase R in red blood cells.
  • Understand the the rationale for activation of pyruvate kinase R and pyruvate kinase M2 in sickle cell nephropathy.
  • Raise awareness of ongoing trials to study the effects of pyruvate kinase in sickle cell disease.

Presentations:

  • 4:50 PM - 5:05 PM ET
    Development of Rilzabrutinib for Patients with SCD

    Presenter: Ahmed Daak, MD, MSc, PhD, DPM, FFPM, EMBA – Sanofi

    Presenter: Rahul Bohra, MD

  • 5:05 PM - 5:20 PM ET
    CSL Behring Presentation

    Presenter: Gregory J. Kato, MD – CSL

  • 5:20 PM - 5:35 PM ET
    Pfizer Rare Disease Sickle Cell Disease Pipeline

    Presenter: Gregory DiRusso, MD – Pfizer

  • 5:35 PM - 5:50 PM ET
    Journavx Presentation

    Presenter: Mac McMillan, PharmD – Your Health Pharmacy

  • 5:50 PM - 6:05 PM ET
    Vasceptor® (Transdermal Curcumin Gel) - A Non-Opioid Drug Candidate with Potent Analgesic and Anti-Inflammatory Properties for Sickle Cell Disease

    Presenter: Mark Diamond, BA – Vascarta Inc.

  • 6:05 PM - 6:20 PM ET
    Agios Presentation

    Presenter: Michael Callaghan, MD – Agios Pharmaceuiticals